Developing a repurposed medicine for Duchenne muscular dystrophy

Repurposing is taking a drug which is already approved for one disease and using it to treat another. Drugs which have been developed or approved for other uses have already been tested in humans, so detailed information is available on their pharmacology, formulation and potential toxicity. Because repurposing/repositioning builds upon previous research and development efforts, new candidate therapies could be ready for clinical trials quickly, speeding their review by Regulatory Authorities and, if approved, their integration into treatment for Duchenne.