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Randomized, controlled trial of miglustat in Gaucher's disease type 3

  • R. Schiffmann
  • , E.J. FitzGibbon
  • , C. Harris
  • , C. DeVile
  • , E.H. Davies
  • , L. Abel
  • , I.N. Van Schaik
  • , W.S. Benko
  • , M. Timmons
  • , M. Ries
  • , A. Vellodi

    Research output: Contribution to journalArticlepeer-review

    Original languageEnglish
    Pages (from-to)514-522
    JournalAnnals of Neurology
    Volume64
    Issue number5
    DOIs
    Publication statusPublished - 1 Nov 2008

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